Genetic, Enzyme, or Protein Disorder: Replacement, Modifiers, Treatment list

Miglustat

0 available brands

Uridine Triacetate

0 available brands

Cromolyn Sodium

0 available brands

Trofinetide

0 available brands

Hydroxyurea

0 available brands

Nusinersen

0 available brands

Vutrisiran

0 available brands

Obeticholic Acid

0 available brands

Sodium Phenylbutyrate + Taurursodiol

0 available brands

Belzutifan

0 available brands

Pegunigalsidase Alfa

0 available brands